NHS England has announced that the first treatment for sickle cell disease in over 20 years will be rolled out to thousands of patients in England with life-saving benefits.
People with the condition endure severe pain during a ‘sickle cell crisis’ that can occur multiple times per year, often requiring hospital admission so they can be given morphine to control the pain and prevent organ failure which can be fatal. The hereditary condition is much more prevalent among people from African or African-Caribbean origin.
The new drug, known as Crizanlizumab, will be delivered by a transfusion drip and works by binding to a protein in the blood cells to prevent the restriction of blood and oxygen supply that lead to a sickle cell crisis.
Last year, NHS England set up ten new dedicated centres to treat sickle cell disease across the country and patients will be able to access the new treatment through their consultant at one of these clinics.
Amanda Pritchard, NHS chief executive, said the drug deal would help as many as 5,000 people over the next three years to have a much better quality of life. The NHS agreed a deal to make Crizanlizumab available for patients earlier than would have otherwise been possible at a price that is fair for taxpayers.
It is the latest in a line of deals secured by the NHS, including a new cholesterol-busting jab and lung cancer drug last month as well as the world’s most expensive drug which treats spinal muscular atrophy in infants, earlier in the year.
Pritchard said: “This is a historic moment for people with sickle cell disease who will be given their first new treatment in over two decades. This revolutionary treatment will help to save lives, allow patients to have a better quality of life and reduce trips to A&E by almost half. The NHS has agreed a deal for this drug, so we are able to provide the latest and best possible treatments for patients at a price that is affordable for taxpayers.”